Supplementary materials.docx (266.98 kB)
Supplementary materials: Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.docx
dataset
posted on 2021-11-18, 13:33 authored by Craig McDonaldCraig McDonald, Francesco MuntoniFrancesco Muntoni, Vinay Penematsa, Joel Jiang, Allan Kristensen, Francesco Bibbiani, Elizabeth GoodwinElizabeth Goodwin, Heather Gordish-Dressman, Lauren Morgenroth, Christian WernerChristian Werner, James Li, Richard Able, Panayiota Trifillis, Már Tulinius, On behalf of the Study 019 & CINRG Duchenne Natural History InvestigatorsSupplementary Table 1 Supplementary Table 2 Supplementary Table 3 Supplementary Table 4 Supplementary Table 5 Supplementary Table 6 |
Supplementary Table 7